Conditions We Treat & Potential Novel Gene Therapies

Click any condition to learn more, see available treatments, and find the providers who manage that condition at UK HealthCare.

• Duchenne Muscular Dystrophy (DMD)
  • Elevidys (delandistrogene moxeparvovec)
• Spinal Muscular Atrophy
  • Zolgensma® (onasemnogene abeparvovec)
  • Spinraza® (nusinersen)
  • Itvisma® (onasemnogene abeparvovec)
• Ear, Nose & Throat
  • Papzimeos® (zopapogene imadenovec-drba)
• Cancer
  • Bladder Cancer
    • Adstiladrin® (nadofaragene firadenovec)
    • Anktiva® (nogapendekin alfa inbakicept)
  • CAR-T Cell therapy:
    • Abecma® (idecabtagene vicleucel)
    • Aucatzyl® (obecabtagene autolucel)
    • Breyanzi® (lisocabtagene maraleucel)
    • Yescarta® (axicabtagene ciloleucel)
    • Kymriah® (tisagenlecleucel)
    • Tecartus® (brexucabtagene autoleucel)
    • Tecelra® (afamitresgene autolucel)
    • Carvykti® (ciltacabtagene autoleucel)
  • BiTE and other specialized infusion therapies
    • Epkinly® (epcoritamab)
    • Blincyto® (blinatumomab)
    • Kimmtrak® (tebentafusp)
    • Tecvayli® (teclistamab)
    • Talvey® (talquetamab)
    • Elrexfio® (elranatamab)